Intern, Clinical Science (Sanfilippo B enzyme replacement therapy)

Location:  San Rafael, California Category: Clinical Employment Category: Fulltime-Temporary


BioMarin is the world leader in delivering therapeutics that provide meaningful advances to patients who live with serious and life-threatening rare genetic diseases. We target diseases that lack effective therapies and affect relatively small numbers of patients, many of whom are children. These conditions are often inherited, difficult to diagnose, progressively debilitating and have few, if any, treatment options. BioMarin will continue to focus on advancing therapies that are the first or best of their kind.

BioMarin’s Research & Development group is responsible for everything from research and discovery to post-market clinical development. Research & Development involves all bench and clinical research and the associated groups that support those endeavors. Our teams work on developing first-in-class and best-in-class therapeutics that provide meaningful advances to patients who live with rare diseases. Come join our team and make a meaningful impact on patients’ lives. 

Our internship program is designed to actively engage students in applying their talents and academic experience in areas of specific professional interest at BioMarin. Our summer interns not only gain hands-on, relevant industry experience, but are also given opportunities to acclimate to the corporate setting through a series of learning workshops, which are designed to prepare them for entering the workforce. The program will begin in mid June and will continue through early September, depending on the candidate’s academic schedule.

All interns must be currently enrolled in an undergraduate or graduate program working towards a degree (certificate programs do not qualify) with plans to enroll in school the following semester. 

Intern Project Description:

This position will consist of an assignment to the ongoing Sanfilippo Syndrome Type B clinical-stage development program. The experience will potentially involve 1) research/literature review to explore aspects of Sanfilippo B pertaining to drug development, and 2) data review, analysis and generation of data outputs relevant to the clinical program. The objective is for the intern to gain insight into the challenges of performing clinical trials in rare diseases; to gain experience evaluating and analyzing clinical trial data; and for the intern to learn effective ways of summarizing and presenting their work. This internship will culminate in a written report and/or oral presentation. Depending on the interest and aptitude of the candidate and meeting schedule, attendance at a scientific meeting or medical advisory board may be included.

Preferred Qualifications:

The candidate should be currently pursuing an undergraduate or graduate degree in the life sciences, medicine or pharmacy and have a demonstrated ability to perform literature research in an academic capacity in order to gather and organize information for the project in question. He or she will need to be familiar and skilled with word processing and spreadsheet applications (Word and Excel) and online search tools and possess excellent communication skills in order to describe findings in a written manner and in an oral presentation (Powerpoint). The candidate will need to have a personable, dynamic, flexible and thoughtful approach.
Skills the intern will gain: The intern will gain an appreciation of the skills required to be successful as a scientist or physician in a dynamic and entrepreneurial biotechnology company. The intern will also gain an appreciation of the complexities associated with understanding how to diagnose, treat and develop novel therapies for children and adults with rare diseases.

Pursuing undergraduate or graduate degree in life sciences or related field.
Work Schedule:  40 hours/week



The employee may frequently be required to sit and talk or hear.  The employee is occasionally required to stand; walk; use hands to finger, handle, or feel; reach with hands and arms; climb or balance; stoop, kneel, crouch, or crawl and taste or smell.  The employee must occasionally lift and/or move up to 25 pounds.  Specific vision abilities by this job include close vision, depth perception and ability to adjust focus.

We are an equal opportunity employer and all qualified applicants will receive consideration for employment without regard to race, color, religion, sex, national origin, disability status, protected veteran status, or any other characteristic protected by law.