Open Positions

Business Development

Sr, Manager, Business Development and Corporate Strategy San Rafael, California
Sr. Manager, Business Development - Strategic Mapping San Rafael, California

Clinical

Associate Director - Biomarker Operations, Clinical Laboratory & Biospecimen Management San Rafael, California
Associate Director, Global Study Operations San Rafael, California
Director, Site Contracts Lead, Strategic R&D Business Operations San Rafael, California
Director, Site Contracts Lead, Strategic R&D Business Operations UK - Also open in the US London, United Kingdom
Head of Early Programs remote, United States
Manager, Development Sciences Business Operations San Rafael, California
Senior Medical Director, Early Clinical Development London, United Kingdom
Sr. Study Manager/Study Manager, Global Study Operations - US (Also open in UK) San Rafael, California
Sr. Study Manager/Study Manager, Global Study Operations UK - Also open in the US London, United Kingdom
Study Specialist II/Sr. Study Specialist San Rafael, California
Study Specialist II/Sr. Study Specialist - US (Also open in UK) San Rafael, California
Study Specialist II/Sr. Study Specialist UK - Also open in US London, United Kingdom
Vendor Contract Manager - UK (also open in the US) London, United Kingdom

Commercial Operations

Associate Director, Digital Marketing – VOXZOGO & ERTs San Rafael, California
Associate Director, Global Training Content Lead, Disease State, Product, Value and Access San Rafael, California
Associate Director, Hemophilia Gene Therapy, Global Marketing San Rafael, California
Associate Director, Market Access remote, Australia
Associate Director, Marketing and Launch Excellence San Rafael, California
Associate Director, Marketing, Cross-Portfolio Strategy - Global Product Strategy San Rafael, California
Associate Director, US Field Therapy Access Manager, Hemophilia remote, United States
Director Marketing, VOXZOGO San Rafael, California
Director, Digital Media & Marketing, Global Digital Strategy & Transformation San Rafael, California
Director, Early Pipeline / BD, Pricing and Policy Research - UK (also open in US) remote, United States
Director, Global Training Content Lead, Disease State, Product, Value and Access, Global Product Strategy San Rafael, California
Director, US Field Reimbursement San Rafael, California
Director, US Hemophilia Patient Marketing Lead San Rafael, California
Intern, Commercial Operations - Brazil Sao Paulo, Brazil
Project Coordinator Haemophilia Kronberg/Ts., Germany
Senior Director, Marketing and Launch Excellence San Rafael, California
Senior Field Clinical Coordinator PKU/ACH; Pittsburgh area remote, United States
Senior Field Clinical Coordinator – PKU/Achondroplasia – Northern CA, AZ remote, United States
Sr. Account Manager, Skeletal Dysplasia, Ohio remote, United States
Sr. Director, Omnichannel Operations San Rafael, California
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Compliance

Director, Compliance Counsel, Global Compliance and Ethics San Rafael, California
EHS&S , Specialist I San Rafael, California
Sr. Manager, GxP Compliance - Regulatory Inspection Management Cork, Ireland

Corporate

Senior Manager, Business Continuity Management - Ireland (also open in US) Cork, Ireland

Data Science

Associate director, Quantitative Science (Data Science/Statistics) San Rafael, California
Associate Director, Quantitative Science - UK (also open in the US) London, United Kingdom
Associate Director, Quantitative Science - US (Also opened in UK) San Rafael, California
Director, Quantitative Science (Post - Approval) San Rafael, California
Senior Clinical Programmer Brisbane, California
Senior Manager, Data Management Science San Rafael, California
Senior Manager, Data Management Science London, United Kingdom
Senior Manager, Statistical Science Brisbane, California

ERP

Associate Director, Global Business Data Leader - Plan to Produce/Material remote, United States
Associate Director, Global Process Leader - Forecast to Plan remote, United States

Facilities

Capital Project Delivery Manager Cork, Ireland
Director, Facilities & Engineering (Non GxP) San Rafael, California
Maintenance Mechanic 2 (Graveyard Shift) Novato, California
Sr. Engineer, Facilities and Utilities Novato, California
Sr. Maintenance Mechanic 1 Novato, California

Finance

Manager, Finance Strategy San Rafael, California
Senior Finance Manager Corporate FP&A remote, United States
Sr. Financial Analyst - Corporate FP&A San Rafael, California
Tax Manager/ Senior Manager Cork, Ireland

Human Resources

Director Employee Relations Novato, California
Executive Director & Head of Diversity, Equity and Inclusion San Rafael, California

Information Technology

IT Senior Business Partner, Manufacturing Systems and Data Strategy Novato, California
IT Solutions Delivery Lead, R&D Operations remote, United States
Principal Application Lead, IT Strategic Platforms, VEEVA remote, United States
Senior Application Lead, IT Strategic Platforms, VEEVA London, United Kingdom
Systems Engineer, Scientific Computing Platforms San Rafael, California
Technology Architect - Integration Domain remote, United States

Legal / Government Affairs

Corporate Counsel San Rafael, California
Senior Manager, Fiscal & Legislative Impact Analysis & Advocacy - Remote Role remote, United States

Manufacturing

Area Lead (Night Shift) Novato, California
Area Lead, Manufacturing (Day Shift) Novato, California
Associate Director, Operational Excellence Novato, California
Bioprocess Specialist - Drug Product Cork, Ireland
Bioprocess Specialist 1, Manufacturing Novato, California
Bioprocess Specialist 2, Manufacturing Novato, California
Biotechnician Cork, Ireland
Drug Product Team Lead Cork, Ireland
Graduate Engineer/ Scientist Cork, Ireland
Manager, Learning Community Novato, California
Manufacturing Associate Novato, California
Material Handler Novato, California
Material Handler II Novato, California
Specialist 1, CAD Novato, California
Specialist, Supply Chain Operations remote, United Kingdom
Sr. Manager, Manufacturing Investigations Novato, California
Supervisor, Manufacturing (Swing Shift) Novato, California

Manufacturing Science and Technology

Manager/Sr Manager Global MSAT Process Validation Dublin, Ireland
Process Steward Cork, Ireland
Research Associate 2, Global MSAT Gene Therapy Center of Excellence Novato, California
Research Associate I, Global MSAT Gene Therapy Center of Excellence Novato, California
Senior Manager, Biologics Centre of Excellence Cork, Ireland

Marketing

Associate Director, Marketing Achondroplasia - ICON Sao Paulo, Brazil
Senior Associate, Marketing - AMEA Dubai, United Arab Emirates

Medical Affairs

Director, Integrated Evidence Planning Excellence San Rafael, California
EU Regional Medical Lead ERT Dubai, United Arab Emirates
Executive Medical Director, US Medical Lead, Hemophilia San Rafael, California
Medical Science Liaison remote, France
Medical Science Liaison (MSL) - Nordics and BeneLux remote, Sweden
Medical Science Liaison - Italy Italy
Medical Scientific Director (Associate Director) - UK (also open in US) London, United Kingdom
Medical Scientific Director (Associate Director) - UK (also open in US) London, United Kingdom

Procurement

Sr. Manager - Global Category Manager CMO/CDMO remote, United States

Product Development

Project Manager II San Rafael, California
Sr. Scientist 1, Chemical, Drug Product and Device Technologies Dublin, Ireland
Sr. Scientist 1, Chemical, Drug Product and Device Technologies Novato, California

Quality

Associate 1, QC Novato, California
Associate 1, QC Novato, California
Associate Director, QC Microbiology Novato, California
Director, Product Quality Leader remote, United States
Lead, QC Analytical Novato, California
QA Senior Associate, External Quality Operations Cork, Ireland
QC Analyst, Critical Reagent and Reference Standard Inventory Management Novato, California
QC Product Analyst (Day Position) Cork, Ireland
QC Senior Associate Cork, Ireland
Technical Manager, External Quality Beykoz/Istanbul, Turkey

Regulatory

Director/Senior Director GRL, Regulatory Affairs San Rafael, California
Manager, Regulatory Global Labeling San Rafael, California
Senior Director (In Vitro Diagnostics and Medical Devices) Regulatory Affairs, CMC San Rafael, California
Sr Manager, Regulatory CMC San Rafael, California
Sr. Associate, Regulatory Affairs San Rafael, California

Research

Director, Clinical Immunology San Rafael, California
Medical Director, Clinical Science - Neuromuscular Disease, UK (Also open in the US) London, United Kingdom
Project Manager II - Early Development Team (EDT), Translational Sciences San Rafael, California
Research Associate II, Assay Strategy and Development San Rafael, California
Research Associate II, Molecular Medicine, Translational Sciences San Rafael, California
Scientist 2, Assay Strategy & Development San Rafael, California
Scientist 2, Statistical Genetics remote, United States
Senior Research Associate 2, Cardiac Cell Biology San Rafael, California
Sr Director, Regulatory Toxicology remote, United States
Sr Nonclinical Study Manager II with experience in GLP Toxicology Studies San Rafael, California
Sr Scientific Manager, Vivarium - IACUC Administration Petaluma, California

Safety & Pharmacovigilance

Medical Writer 2 San Rafael, California
Medical Writer 2 San Rafael, California
Medical Writer 2 San Rafael, California

Supply Chain

Sr. Manager, Network Capacity Management remote, United States

Technical Development

Project Manager, CMC Operations Novato, California
Research Associate 2 Novato, California
Scientist 2, Analytical Sciences Novato, California
Scientist 2, Analytical Sciences - Molecular Biology Novato, California
Scientist 2, Upstream Process Development Novato, California
Specialist 1, Pilot Plant Manufacturing Novato, California
Specialist 2, Pilot Plant Manufacturing Novato, California
Sr. Scientist 1, Analytical Sciences Novato, California
Supervisor, Gene Therapy Pilot Plant Novato, California

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